Biochemistry, Genetics and Molecular Biology
CRISPR
100%
GM2 Gangliosidoses
100%
Genome Editing
100%
Tay-Sachs Disease
100%
Fibroblast
100%
Chimeric Protein
100%
Wild Type
66%
Hexosaminidase
33%
CRISPR/Cas9
33%
GM2 (Ganglioside)
33%
Gene Therapy
33%
AAVS1
33%
Immune Response
33%
Mitochondrion
33%
Immunity
33%
Enzyme Activity
33%
Transfection
33%
Sandhoff Disease
33%
Plasmid
33%
Lipofection
33%
INIS
diseases
100%
fibroblasts
100%
proteins
75%
humans
50%
mutations
50%
genes
25%
patients
25%
mitochondria
25%
enzyme activity
25%
interfaces
25%
storage
25%
in vitro
25%
culture media
25%
gene therapy
25%
corrections
25%
plasmids
25%
gangliosides
25%
time dependence
25%
albumins
25%
harbors
25%
extracellular space
25%
Pharmacology, Toxicology and Pharmaceutical Science
Tay Sachs Disease
100%
GM2 Gangliosidoses
100%
Chimeric Protein
100%
Diseases
100%
Lysosome Storage Disease
33%
Sandhoff Disease
33%
Ganglioside GM2
33%
Beta N Acetylhexosaminidase A
33%
Homodimer
33%
Beta N Acetylhexosaminidase B
33%
Keyphrases
Chimeric Protein
100%
Therapy Approaches
33%
Lipofection
33%
Mitochondria-dependent
33%
Cross-correction
33%
Donor Plasmid
33%
GM2AP
33%
Safe Harbor
33%
Mass-dependent
33%
Human Immune System
33%