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Magnetoliposomes as Carriers for CRISPR/nCas9-Based Gene Therapy on In Vitro Models of Mucopolysaccharidoses IVA and GM2 Gangliosidoses: Proof-of-Concept Experiments

Research output: Contribution to journalMeeting Abstractpeer-review

Original languageEnglish
Pages (from-to)475-476
Number of pages2
JournalMolecular Therapy
Volume30
Issue number4
StatePublished - Apr 2022

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